Muscular Dystrophy

Gene Therapy Strategies for Muscular Dystrophies: Current Insights and Future Directions

This review article provides an in-depth overview of gene therapy modalities — including gene replacement, gene editing, and gene inactivation — and how these strategies are shaping the future of muscular dystrophy treatment....
Read More

Toward an AAV Gene Therapy to Treat Muscular Dystrophies

New innovations in AAV vector engineering — including dual-vector methods and enhanced tissue targeting — are opening doors for treating muscular dystrophies once considered untreatable....
Read More